Prion Disease Treatment: Milestone in Gene-Editing Therapy

April 7, 2025

Prion disease treatment has taken a significant leap forward, thanks to groundbreaking research that shines a hopeful light on these rare, yet devastating disorders.In a recent study published in *Nature Medicine*, scientists have developed a promising gene-editing therapy capable of reducing the toxic prion protein production in the brains of laboratory mice, which extended their lives by an impressive 52 percent.
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